Browsing Molekulare Medizin by Author "Jakubiczka-Smorag, Joanna"
Now showing items 1-1 of 1
-
rAAV-based gene therapy for molybdenum cofactor deficiency type B
Jakubiczka-Smorag, Joanna (2015-06-29)Molybdenum cofactor (MoCo) deficiency type A is thus far only one curable type of MoCo deficiency. In the present study, a mouse model for MoCo deficiency type B (Mocs2-/-) was generated, characterised and used for preclinical ...